Status | Study |
Recruiting |
Study Name: Characterization of Patients With Tuberous Sclerosis Complex, Lymphangioleiomyomatosis and Angiomyolipoma Condition: Tuberous Sclerosis Lymphangioleiomyomatosis Angiomyolipoma Date: 2014-12-14 |
Recruiting |
Study Name: A Pilot Study To Evaluate The Effects of Everolimus on Brain mTOR Activity and Cortical Hyperexcitability in TSC and FCD Condition: Epilepsy Tuberous Sclerosis Complex Focal Cortical Dysplas Date: 2014-10-08 Interventions: Drug: Everolimus This study will measure if the drug called Everolimus effects mTOR signaling (an electr |
Recruiting |
Study Name: Everolimus for Cancer With TSC1 or TSC2 Mutation Condition: TSC1 TSC2 Tuberous Sclerosis Complex Date: 2014-07-23 Interventions: Drug: Everolimus Other Names: Afinitor® Zortress |
Recruiting |
Study Name: Treatment of Renal Angiomyolipomas in Tuberous Sclerosis by Beta-blockers Condition: Renal Angiomyolipomas Tuberous Sclerosis Date: 2014-04-01 Interventions: Drug: Propranolol |
Recruiting |
Study Name: Safety of Simvastatin in LAM and TSC Condition: Lymphangioleiomyomatosis Tuberous Sclerosis Complex Date: 2014-01-23 Interventions: Drug: Simvastatin Eligible patients will be assigned to receive 20 mg of simvastatin once daily for a pe |
Recruiting |
Study Name: A Study of Everolimus in the Treatment of Neurocognitive Problems in Tuberous Sclerosis Condition: Tuberous Sclerosis Date: 2013-09-05 Interventions: Drug: Placebo 5mg daily admini |
Active, not recruiting |
Study Name: Early Biomarkers of Autism in Infants With Tuberous Sclerosis Complex (TSC) Condition: Tuberous Sclerosis Complex Date: 2013-01-28 |
Completed |
Study Name: Topical Rapamycin to Erase Angiofibromas in TSC Condition: Angiofibromas Tuberous Sclerosis Date: 2012-02-01 Interventions: Drug: Placebo Study cream is a |
Completed |
Study Name: Trial of RAD001 and Neurocognition in Tuberous Sclerosis Complex (TSC) Condition: Tuberous Sclerosis Complex Date: 2011-02-02 Interventions: Drug: RAD001 RAD001 is formulated as tablets of 5.0 mg str |
Completed |
Study Name: Rapamycin In Angiomyolipomas In Patients With Tuberous Sclerosis Condition: Angiomyolipoma Date: 2010-10-06 Interventions: Drug: Sirolimus plasma levels between 4 and 8 Other |